317. Trifunctional protein deficiency Clinical trials / Disease details


Clinical trials : 3 Drugs : 8 - (DrugBank : 4) / Drug target gene : 1 - Drug target pathway : 1

  
1 trial found
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
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Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
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size
PhaseCountries
1NCT00840112
(ClinicalTrials.gov)
July 20109/2/2009Vitamin E Treatment for Long-Chain 3-Hydroxyacyl Coenzyme A (CoA) Dehydrogenase (LCHAD) Associated NeuropathyVitamin E Treatment for LCHAD Associated NeuropathyPeripheral Neuropathy;Mitochondrial Trifunctional Protein DeficiencyDietary Supplement: Vitamin E supplementOregon Health and Science UniversityNational Institute of Diabetes and Digestive and Kidney Diseases (NIDDK);Oregon State UniversityTerminated7 YearsN/ABoth1N/AUnited States