320. Inherited glycosylphosphatidylinositol deficiency Clinical trials / Disease details

Clinical trials : 3 / Drugs : 2 - (DrugBank : 2) / Drug target gene : 0 - Drug target pathway : 0

2 trials found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	JPRN-jRCTs051180113	01/04/2019	11/03/2019	Novel replacement therapy for inherited GPI deficiency	Novel replacement therapy for inherited GPI deficiency - Novel replacement therapy for inherited GPI ...	Inherited GPI deficiency Inherited GPI deficiency	Folinic acid1mg/kg/day in three divided dose to start. If the 5-MTHF concentration in cerebrospinal ...	Nabatame Shin	NULL	Recruiting	Not applicable	Not applicable	Both	5	N/A	Japan
2	JPRN-UMIN000030314	2019/04/01	15/01/2018	Novel replacement therapy for inherited GPI deficiency (IGD)	Novel replacement therapy for inherited GPI deficiency (IGD) - Novel replacement therapy for inherit ...	Inherited GPI deficiency	Folinic acid1mg/kg/day in three divided dose to start. If the 5-MTHF concentration in cerebrospinal ...	Osaka University	NULL	Recruiting	Not applicable	Not applicable	Male and Female	5	Not selected	Japan

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