65. Primary immunodeficiency Clinical trials / Disease details


Clinical trials : 482 Drugs : 653 - (DrugBank : 119) / Drug target genes : 92 - Drug target pathways : 212

  
2 trials found
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT04870866
(ClinicalTrials.gov)
June 5, 201923/4/2021NAD Supplementation to Prevent Progressive Neurological Disease in Ataxia TelangiectasiaNAD Supplementation to Prevent Progressive Neurological Disease in Ataxia TelangiectasiaAtaxia TelangiectasiaDrug: Nicotinamide ribonucleosideUniversity Hospital, AkershusThe Bergesen Foundation;South-Eastern Norway Regional Health Authority;Sykehuset Innlandet HF;Oslo University Hospital;St. Olavs Hospital;Haukeland University Hospital;University Hospital of North Norway;University of BergenActive, not recruiting3 YearsN/AAll13Phase 2Norway
2NCT03962114
(ClinicalTrials.gov)
March 18, 201911/4/2019Effects of Vitamin B3 in Patients With Ataxia TelangiectasiaEffects of Nicotinamide Riboside (Vitamin B3) in Patients With Ataxia Telangiectasia.Ataxia Telangiectasia;ATM Gene MutationDietary Supplement: Vitamin B3Radboud UniversityA-T childrens project;Twan foundationEnrolling by invitation2 YearsN/AAll24Phase 2Netherlands