Agalsidase beta (recombinant form) ( DrugBank: Agalsidase beta )


1 disease
IDDisease name (Link within this page)Number of trials
19Lysosomal storage disease1

19. Lysosomal storage disease


Clinical trials : 854 Drugs : 716 - (DrugBank : 105) / Drug target genes : 70 - Drug target pathways : 191
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT00233870
(ClinicalTrials.gov)
June 20045/10/2005A Long Term Safety and Efficacy Study of Fabrazyme Replacement Therapy in Japanese Patients With Fabry Disease.Special Survey in Long-Term Use of FabrazymeFabry DiseaseDrug: Agalsidase beta (recombinant form)Genzyme, a Sanofi CompanyNULLCompletedN/AN/ABoth405Japan