Autologous Plasmablasts ( DrugBank: - )


1 disease
IDDisease name (Link within this page)Number of trials
19Lysosomal storage disease1

19. Lysosomal storage disease


Clinical trials : 854 Drugs : 716 - (DrugBank : 105) / Drug target genes : 70 - Drug target pathways : 191
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PhaseCountries
1NCT04284254
(ClinicalTrials.gov)
December 202111/11/2019MT2018-18: Sleeping Beauty Transposon-Engineered Plasmablasts for Hurler Syndrome Post Allo HSCTSleeping Beauty Transposon-Engineered Plasmablasts for Expression and Delivery of Alpha-L-iduronidase in Patients With Hurler Syndrome That Have Previously Undergone Allogeneic TransplantationMucopolysaccharidosis Type IH (MPS IH, Hurler Syndrome);Mucopolysaccharidosis Type IH;MPS IH, Hurler SyndromeDrug: Autologous PlasmablastsMasonic Cancer Center, University of MinnesotaNULLNot yet recruiting3 Years8 YearsAll36Phase 1/Phase 2NULL