Other: Cysteamine bitartrate ( DrugBank: Cysteamine )


1 disease
IDDisease name (Link within this page)Number of trials
19Lysosomal storage disease1

19. Lysosomal storage disease


Clinical trials : 854 Drugs : 716 - (DrugBank : 105) / Drug target genes : 70 - Drug target pathways : 191
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT02012114
(ClinicalTrials.gov)
December 201111/12/2012A Cohort of Patients With Cystinosis : Compliance to Cysteamine and Neurological ComplicationsA Cohort of Patients With Cystinosis : Compliance to Cysteamine and Neurological ComplicationsCystinosisOther: Cysteamine bitartrateHospices Civils de LyonNULLRecruiting4 YearsN/ABoth90N/AFrance