Other: Parts A/B: Sham Control ( DrugBank: - )


1 disease
IDDisease name (Link within this page)Number of trials
19Lysosomal storage disease1

19. Lysosomal storage disease


Clinical trials : 854 Drugs : 716 - (DrugBank : 105) / Drug target genes : 70 - Drug target pathways : 191
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registration
Public_titleScientific_titleConditionInterventionPrimary_
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agemin
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PhaseCountries
1NCT02534844
(ClinicalTrials.gov)
October 201518/8/2015VTS-270 to Treat Niemann-Pick Type C1 (NPC1) DiseaseA Phase 2b/3 Prospective, Randomized, Double-Blind, Sham-Controlled 3-Part Trial of VTS-270 (2-hydroxypropyl-ß-cyclodextrin) in Subjects With Neurologic Manifestations of Niemann-Pick Type C1 (NPC1) DiseaseNiemann-Pick Disease, Type CDrug: Parts A/B: Adrabetadex;Other: Parts A/B: Sham ControlMandos LLCNULLActive, not recruiting4 Years21 YearsAll51Phase 2/Phase 3United States;Australia;France;Germany;New Zealand;Singapore;Spain;Turkey;United Kingdom