Other: Diet ( DrugBank: - )

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1 disease

ID	Disease name (Link within this page)	Number of trials
240	Phenylketonuria	3

240. Phenylketonuria

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Clinical trials : 138 /  Drugs : 106 - (DrugBank : 11) / Drug target gene : 1 - Drug target pathways : 5

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT03820804 (ClinicalTrials.gov)	January 7, 2019	19/10/2018	Nutritional Status in Phenylketonuria	Trends in Nutritional Status of Patients With Phenylketonuria	Phenylketonurias	Other: Diet;Drug: Sapropterin	Universidade do Porto	Centro Hospitalar do Porto;BioMarin Pharmaceutical	Completed	3 Years	N/A	All	94		Portugal
2	NCT02677870 (ClinicalTrials.gov)	January 2018	26/1/2016	The Effectiveness of Kuvan in Amish PKU Patients	The Effectiveness of High-Dose Synthetic BH4 (Saproterin Dihydrochloride or Kuvan) in Amish PKU Patients	Phenylketonuria	Drug: saproterin dihydrochloride;Other: Diet treatment	University Hospitals Cleveland Medical Center	BioMarin Pharmaceutical	Recruiting	2 Years	60 Years	All	25	Phase 4	United States
3	NCT00841100 (ClinicalTrials.gov)	December 2008	10/2/2009	Kuvan Therapy in Phenylketonuria (PKU): The Effect of Blood Phenylalanine Concentration on Kuvan Response	Kuvan Therapy in Phenylketonuria (PKU): The Effect of Blood Phenylalanine Concentration on Kuvan Response	Phenylketonuria	Drug: Kuvan;Other: Diet	University of Miami	NULL	Completed	4 Years	N/A	All	21	Phase 2	United States