Glyceryl tri-(4-phenylbutyrate)(GT4P) ( DrugBank: 4-phenylbutyrate, Phenylbutyrate, GT4P )


1 disease
IDDisease name (Link within this page)Number of trials
251Urea cycle disorder1

251. Urea cycle disorder


Clinical trials : 48 Drugs : 52 - (DrugBank : 13) / Drug target genes : 4 - Drug target pathways : 29
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1EUCTR2008-003865-23-GB
(EUCTR)
08/09/200825/07/2008A Phase 2, Switch-Over, Dose-Escalation Study of the Safety and Tolerability of HPN-100 (glyceryl tri-[4-phenylbutyrate]) Compared to Sodium Phenylbutyrate in Adult and Pediatric Subjects with Urea Cycle DisordersA Phase 2, Switch-Over, Dose-Escalation Study of the Safety and Tolerability of HPN-100 (glyceryl tri-[4-phenylbutyrate]) Compared to Sodium Phenylbutyrate in Adult and Pediatric Subjects with Urea Cycle Disorders Urea Cycle Disorder (urea cycle enzyme or transporter deficiency)
MedDRA version: 9.1;Level: LLT;Classification code 10013373;Term: Disorders of urea cycle metabolism
Product Name: glyceryl tri-(4-phenylbutyrate)(GT4P)
Product Code: HPN-100
INN or Proposed INN: NA
Other descriptive name: glyceryl tri-(4-phenylbutyrate)
Hyperion Therapeutics LimitedNULLNot RecruitingFemale: yes
Male: yes
16Phase 2United Kingdom