Isotopic Intravenous [13C]-Urea ( DrugBank: Urea )


1 disease
IDDisease name (Link within this page)Number of trials
251Urea cycle disorder1

251. Urea cycle disorder


Clinical trials : 48 Drugs : 52 - (DrugBank : 13) / Drug target genes : 4 - Drug target pathways : 29
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1NCT02670889
(ClinicalTrials.gov)
November 201614/1/2016Urease Inhibitor Drug Treatment for Urea Cycle DisordersManipulating the Gut Microbiome in Urea Cycle DisordersOrnithine Transcarbamylase Deficiency;Argininosuccinate Synthetase Deficiency (Citrullinemia);Argininosuccinic Acid Lyase Deficiency (Argininosuccinic Aciduria);Carbamyl-Phosphate Synthase I DeficiencyDrug: Acetohydroxamic Acid;Drug: Isotopic Intravenous [13C]-UreaNicholas Ah MewData Management and Coordinating Center (DMCC);Children's Hospital of PhiladelphiaNot yet recruiting18 Years60 YearsBoth16Phase 1/Phase 2NULL