Transduced CD34+ Cells ( DrugBank: - )


1 disease
IDDisease name (Link within this page)Number of trials
285Fanconi anemia1

285. Fanconi anemia


Clinical trials : 59 Drugs : 118 - (DrugBank : 32) / Drug target genes : 31 - Drug target pathways : 155
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enrollment
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registration
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agemin
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agemax
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PhaseCountries
1NCT00001399
(ClinicalTrials.gov)
December 3, 19933/11/1999Gene Therapy for the Treatment of Fanconi's Anemia Type CRetroviral Mediated Gene Transfer of the Fanconi Anemia Complementation Group C Gene to Hematopoietic Progenitors of Group C PatientsFanconi's Anemia;PancytopeniaDrug: Transduced CD34+ CellsNational Heart, Lung, and Blood Institute (NHLBI)NULLCompleted5 YearsN/AAll9Phase 1United States