COL7A1-SIN retroviral vector engineered autologous tissue-engineered skin ( DrugBank: - )


1 disease
IDDisease name (Link within this page)Number of trials
36Epidermolysis bullosa1

36. Epidermolysis bullosa


Clinical trials : 160 Drugs : 195 - (DrugBank : 47) / Drug target genes : 50 - Drug target pathways : 124
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1NCT04186650
(ClinicalTrials.gov)
January 10, 202025/11/2019Ex Vivo Gene Therapy Clinical Trial for RDEB Using Genetically Corrected Autologous Skin Equivalent GraftsPhase I/II ex Vivo Gene Therapy Clinical Trial for RDEB Using Autologous Skin Equivalent Grafts Genetically Corrected With a COL7A1-encoding SIN Retroviral VectorEpidermolysis Bullosa Dystrophica, RecessiveBiological: COL7A1-SIN retroviral vector engineered autologous tissue-engineered skinInstitut National de la Santé Et de la Recherche Médicale, FranceNULLActive, not recruiting18 YearsN/AAll3Phase 1/Phase 2France