Other: Observational ( DrugBank: - )


1 disease
IDDisease name (Link within this page)Number of trials
90Retinitis pigmentosa1

90. Retinitis pigmentosa


Clinical trials : 130 Drugs : 180 - (DrugBank : 41) / Drug target genes : 49 - Drug target pathways : 109
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
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size
PhaseCountries
1NCT04517149
(ClinicalTrials.gov)
June 9, 202014/8/20204D-125 in Patients With X-Linked Retinitis Pigmentosa (XLRP)An Open-label, Phase 1/2 Trial of Gene Therapy 4D-125 in Males With X-linked Retinitis Pigmentosa (XLRP) Caused by Mutations in the RPGR GeneX-Linked Retinitis PigmentosaBiological: 4D-125 IVT Injection;Other: Observational4D Molecular TherapeuticsNULLRecruiting18 YearsN/AMale43Phase 1/Phase 2United States