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13 / 17,542 descriptions

No. Drug (Description in trials) DrugBank KEGG DRUG KEGG GENES KEGG PATHWAY
On map, Yellow: Drug target genes
Disease ID
 1  Ataluren  Ataluren  [1] D09323 💬  [6] 19, 113, 140, 246, 299, 329 💬 
 2  Ataluren (ptc124®)  Ataluren  [1] D09323 💬  [1] 299 💬 
 3  Ataluren 1000 mg  Ataluren  [1] D09323 💬  [1] 113 💬 
 4  Ataluren 1000mg  Ataluren  [1] D09323 💬  [1] 246 💬 
 5  Ataluren 125 mg  Ataluren  [1] D09323 💬  [1] 113 💬 
 6  Ataluren 125mg  Ataluren  [1] D09323 💬  [1] 246 💬 
 7  Ataluren 250 mg  Ataluren  [1] D09323 💬  [1] 113 💬 
 8  Ataluren 250mg  Ataluren  [1] D09323 💬  [1] 246 💬 
 9  Ivacaftor/ataluren  Ataluren  [2] D09323, D09916 💬  [1] CFTR 💬  [8] ABC transporters, AMPK signaling pathway, Bile secretion, Gastric acid secretion, Pancreatic secretion, Tight junction, Vibrio cholerae infection, cAMP signaling pathway  [1] 299 💬 
 10  Translarna  [1] 113 💬 
 11  Translarna 1000 mg granules for oral suspension  [1] 113 💬 
 12  Translarna 125 mg granules for oral suspension  [1] 113 💬 
 13  Translarna 250 mg granules for oral suspension  [1] 113 💬