3. Spinal muscular atrophy
179 clinical trials,   102 drugs   (DrugBank: 26 drugs),   52 drug target genes,   78 drug target pathways

Searched query = "Spinal muscular atrophy", "Myelopathic muscular atrophy", "SMA I", "Werdnig-Hoffman disease", "SMA II", "Dubowitz disease", "SMA III", "Kugelberg-Welander disease", "SMA IV"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: 03/15/2021. Trials are sorted by Date_enrollment from most recent to oldest in the table.

Search in Page e.g. "Phase 3", "Not recruiting", "Japan"
3 trials found
No.TrialIDDate_
enrollment
Date_
registration
Public_titleScientific_titleConditionInterventionPrimary_
sponsor
Secondary_
sponsor
Recruitment_
Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
Target_
size
PhaseCountries
1NCT00439569
(ClinicalTrials.gov)
January 200821/2/2007Clinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Types II or IIIPhase I/IIa Clinical Trial of Sodium Phenylbutyrate in Pediatric Subjects With Type II/III Spinal Muscular AtrophySpinal Muscular Atrophy Type II;Spinal Muscular Atrophy Type IIIDrug: sodium phenylbutyrateWestatNational Institute of Neurological Disorders and Stroke (NINDS)Terminated2 Years11 YearsAll9Phase 1;Phase 2United States
2NCT00439218
(ClinicalTrials.gov)
January 200822/2/2007Clinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Type IPhase I/IIa Clinical Trial of Sodium Phenylbutyrate in Pediatric Subjects With Type I Spinal Muscular AtrophySpinal Muscular Atrophy Type IDrug: sodium phenylbutyrateWestatNational Institute of Neurological Disorders and Stroke (NINDS)Terminated2 Months48 MonthsAll5Phase 1;Phase 2United States
3NCT00528268
(ClinicalTrials.gov)
July 200710/9/2007Study to Evaluate Sodium Phenylbutyrate in Pre-symptomatic Infants With Spinal Muscular AtrophyProspective Phase I/II Study to Evaluate Effects of Sodium Phenylbutyrate in Pre-symptomatic Infants With Spinal Muscular AtrophySpinal Muscular AtrophyDrug: Sodium phenylbutyrate (NaPB)University of UtahEunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)CompletedN/A6 MonthsAll14Phase 1;Phase 2United States