A Phase I/II clinical trial of hematopoietic stem cell gene therapy for the treatment of Metachromatic Leukodystrophy - TIGET-MLD A Phase I/II clinical trial of hematopoietic stem cell gene therapy for the treatment of Metachromat ...
A Phase I/II clinical trial of hematopoietic stem cell gene therapy for the treatment of Metachromatic Leukodystrophy - TIGET-MLD A Phase I/II clinical trial of hematopoietic stem cell gene therapy for the treatment of Metachromat ...
Product Name: autologous CD34+ cells transduced with a lentiviral vector encoding the ARSA cDNA Trade Name: BUSILVEX INN or Proposed INN: Busulfan Product Name: autologous CD34+ cells transduced with a lentiviral vector encoding the ARSA cDNA Trade ...