A Gene Therapy Study in Patients With Gaucher Disease Type 1
A Phase 1/2, Open-label, Safety, Tolerability, and Efficacy Study of FLT201 in Adult Patients With Gaucher Disease Type 1 (GALILEO-1) A Phase 1/2, Open-label, Safety, Tolerability, and Efficacy Study of FLT201in Adult Patients With Ga ...