Safety Study of a Gene Transfer Vector for Children With Late Infantile Neuronal Ceroid Lipofuscinosis Safety Study of a Gene Transfer Vector for Children With Late Infantile Neuronal Ceroid Lipofuscinos ...
Administration of a Replication Deficient Adeno-associated Virus Gene Transfer Vector Expressing the Human CLN2 cDNA to the Brain of Children With Late Infantile Neuronal Ceroid Lipofuscinosis Administration of a Replication Deficient Adeno-associated Virus Gene Transfer Vector Expressing the ...