Autologous CD34+ HSCs transduced ex vivo with CD11B LV encoding human IDS tagged with ApoEII

( DrugBank: - / KEGG DRUG: - )

1 disease

告示番号	疾患名（ページ内リンク）	臨床試験数
19	ライソゾーム病	1

19. ライソゾーム病

臨床試験数 : 899 / 薬物数 : 684 - (DrugBank : 99) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 182

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT05665166 (ClinicalTrials.gov)	February 2023	7/12/2022	Autologous Ex-vivo Gene Modified HSCT in MPSII	A Phase I/II, Study of Autologous CD34+Haematopoietic Stem Cells Transduced ex Vivo With CD11BLentiv ...	Mucopolysaccharidosis II	Genetic: Autologous CD34+ HSCs transduced ex vivo with CD11B LV encoding human IDS tagged with ApoEI ...	University of Manchester	Manchester University NHS Foundation Trust;AVROBIO;CTI Clinical Trial and Consulting Services;Great ...	Not yet recruiting	3 Months	12 Months	Male	5	Phase 1/Phase 2	NULL

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