Extension Study of Intrathecal Enzyme Replacement for Cognitive Decline in MPS I
An Extension Study of Intrathecal Enzyme Replacement for Cognitive Decline in Mucopolysaccharidosis I An Extension Study of IntrathecalEnzyme Replacement for Cognitive Decline in Mucopolysaccharidosis I ...
Mucopolysaccharidosis I;Cognitive Decline
Drug: Intrathecalrecombinanthumanalphaiduronidase
agnes chen
University of Minnesota;UCSF Benioff Children's Hospital Oakland;University of California, Los Angeles;The Ryan Foundation;Rare Diseases Clinical Research Network;National Institute of Neurological Disorders and Stroke (NINDS) University of Minnesota;UCSF Benioff Children's Hospital Oakland;University of California, Los Angel ...