Efficacy METAZYM for the Treatment Metachromatic Leukodystrophy Treated With Hematopoietic Stem Cell Transplantation Efficacy METAZYM for the Treatment Metachromatic Leukodystrophy Treated With Hematopoietic Stem Cell ...
and Safety of METAZYM (Recombinant Human Arylsulfatase A or rhASA) for the Treatment of Patients With Late Infantile MLD Who Had Previously Hematopoietic Stem Cell Transplantation and Safety of METAZYM (Recombinant Human Arylsulfatase A or rhASA) for the Treatment of Patients Wit ...
Metachromatic Leukodystrophy
Drug: rhARSA
Assistance Publique - Hôpitaux de Paris
European Leukodystrophy Association;Zymenex A/S;Shire