A first-in-human study of UX053 in Patients with Glycogen Storage Disease type III (GSD III)
A Phase 1/2 First-in-human, 2-part Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of Single Ascending Doses (Part 1: Open-label) and Repeat Doses (Part 2: Randomized, Double-blind, Placebo-controlled) of UX053 in Patients with GSD III - UX053-CL101 A Phase 1/2 First-in-human, 2-part Study to Evaluate the Safety, Tolerability, and Pharmacokinetics ...
Glycogen Storage Disease Type III (GSD III) MedDRA version: 20.1;Level: PT;Classification code 10053250;Term: Glycogen storage disease type III;System Organ Class: 10010331 - Congenital, familial and genetic disorders;Therapeutic area: Diseases [C] - Nutritional and Metabolic Diseases [C18] Glycogen Storage Disease Type III (GSD III) MedDRA version: 20.1;Level: PT;Classification code 10053 ...
Product Name: mRNA che codifica l’enzima umano deramificante del glicogeno formulato in una nanopaticella lipidica Product Code: [UX053] Product Name: dexamethasone (or equivalent) Product Code: [-] Product Name: mRNA che codifica l’enzima umano deramificante del glicogeno formulato in una nanopati ...
A first-in-human study of UX053 in Patients with Glycogen Storage Disease type III (GSD III)
A Phase 1/2 First-in-human, 2-part Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of Single Ascending Doses (Part 1: Open-label) and Repeat Doses (Part 2: Randomized, Double-blind, Placebo-controlled) of UX053 in Patients with GSD III A Phase 1/2 First-in-human, 2-part Study to Evaluate the Safety, Tolerability, and Pharmacokinetics ...
Glycogen Storage Disease Type III (GSD III) MedDRA version: 20.1;Level: PT;Classification code 10053250;Term: Glycogen storage disease type III;System Organ Class: 10010331 - Congenital, familial and genetic disorders;Therapeutic area: Diseases [C] - Nutritional and Metabolic Diseases [C18] Glycogen Storage Disease Type III (GSD III) MedDRA version: 20.1;Level: PT;Classification code 10053 ...
Product Name: mRNA encoding the human glycogen debranching enzyme formulated in a lipid nanoparticle delivery Product Code: UX053 INN or Proposed INN: Not yet available Other descriptive name: mRNA encoding the human glycogen debranching enzyme Product Name: mRNA encoding the human glycogen debranching enzyme formulated in a lipid nanoparticle ...
Safety, Tolerability, and Pharmacokinetics of UX053 in Patients With Glycogen Storage Disease Type III (GSD III) Safety, Tolerability, and Pharmacokinetics of UX053in Patients With Glycogen Storage Disease Type II ...
A Phase 1/2 First-in-human, Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of Single Ascending Doses and Repeat Doses of UX053 in Patients With GSD III A Phase 1/2 First-in-human, Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of Sing ...