Nutritional and Neurotransmitter Changes in PKU Subjects on BH4
Baseline Evaluation and Long-term Follow-up of Nutritional Status and Neurotransmitter Concentrations in Phenylketonuria Patients Initiating Treatment With Sapropterin Dihydrochloride (KuvanTM), a Tetrahydrobiopterin Analog. Baseline Evaluation and Long-term Follow-up of Nutritional Status and Neurotransmitter Concentration ...
Phenylketonuria
Drug: KuvanTMTherapy
Emory University
BioMarin Pharmaceutical;Atlanta Clinical and Translational Science Institute