A Phase 3 Study of UX003 RecombinantHumanBetaglucuronidase (rhGUS) Enzyme Replacement Therapy in Patients With Mucopolysaccharidosis Type 7 (MPS 7) A Phase 3 Study of UX003 RecombinantHumanBetaglucuronidase(rhGUS) Enzyme Replacement Therapy in Pa ...
A Randomized, Placebo-Controlled, Blind-Start, Single-Crossover Phase 3 Study to Assess the Efficacy and Safety of UX003 rhGUS Enzyme Replacement Therapy in Patients With MPS 7 A Randomized, Placebo-Controlled, Blind-Start, Single-Crossover Phase 3 Study to Assess the Efficacy ...
A safety and efficacy study in young MPS 7 patients (less than 5 years old) receiving enzyme (UX003) replacement by intravenous injection A safety and efficacy study in young MPS 7 patients (less than 5 years old) receiving enzyme (UX003) ...
An Open-label Study of UX003 rhGUS Enzyme Replacement Therapy in MPS 7 Patients Less than 5 years old An Open-label Study of UX003 rhGUS Enzyme Replacement Therapy in MPS 7 Patients Less than 5 years ol ...
Mucopolysaccharidosis type 7 (MPS 7, Sly syndrome);Therapeutic area: Diseases [C] - Congenital, Hereditary, and Neonatal Diseases and Abnormalities [C16] Mucopolysaccharidosis type 7 (MPS 7, Sly syndrome);Therapeutic area: Diseases [C] - Congenital, Here ...
Product Name: Recombinanthumanbetaglucuronidase Product Code: UX003 INN or Proposed INN: pending Other descriptive name: RECOMBINANTHUMAN BETA GLUCURONIDASE; RHGUS Product Name: Recombinanthumanbetaglucuronidase Product Code: UX003 INN or Proposed INN: pending Othe ...