A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)
A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)
Mucopolysaccharidosis IV Type A;Morquio A Syndrome;MPS IVA
Drug: Vimizim®(elosulfasealfa)
BioMarin Pharmaceutical
ICON plc
Active, not recruiting
N/A
N/A
All
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United States;Australia;Austria;Belgium;Canada;Czechia;Denmark;France;Ireland;Italy;Malaysia;Netherlands;Poland;Portugal;Puerto Rico;Taiwan;United Kingdom;Germany United States;Australia;Austria;Belgium;Canada;Czechia;Denmark;France;Ireland;Italy;Malaysia;Netherl ...