30. 遠位型ミオパチー
［臨床試験数：13，薬物数：16（DrugBank：3），標的遺伝子数：1，標的パスウェイ数：1］

Searched query = "Distal myopathy", "Distal muscular dystrophy", "Miyoshi myopathy", "Distal dysferlinopathy", "DMRV/GNE myopathy", "Oculopharyngodistal myopathy"
The queries were searched in Public_title, Scientific_title, and Condition. Export date: . Trials are sorted by Date_enrollment from most recent to oldest in the table.

Drug = ACENEURAMIC ACID; Aceneuramic Acid; Aceneuramic Acid Extended-Release; Aceneuramic Acid Extended-Release Tablets; Aceneuramic acid; Aceneuramic acid extended-release (Ace-ER); Common Name: Sialic Acid; Deflazacort; INN: aceneuramic acid; N-acetylneuraminic acid; NPC-09; SA; Sialic acid; Sialic acid (INN: aceneuramic acid); Sialic acid, N-acetylneuraminic acid; UX001