DDrare
Disease
Drug
Target Gene/Pathway
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Drug
Description in Trials
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Showing 1 to 4 of 4 descriptions
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薬物名(臨床試験情報から抽出)
DrugBank
KEGG DRUG
KEGG GENES
KEGG PATHWAY
指定難病告示番号
1
GALSULFASE
(Synonym:
NAGLAZYME
)
1件:
Galsulfase
Galsulfase
(Synonym:
Naglazyme
)
1件:
D06565
D06565
(Name:
NAGLAZYME
)
1件:
ARSB
ARSB
💬
3件:
Glycosaminoglycan degradation
Glycosaminoglycan degradation
,
Lysosome
,
Metabolic pathways
💬
1件:
19
19
2
Naglazyme
1件:
Galsulfase
Galsulfase
(Synonym:
Naglazyme
)
1件:
D06565
D06565
(Name:
NAGLAZYME
)
1件:
ARSB
ARSB
💬
3件:
Glycosaminoglycan degradation
Glycosaminoglycan degradation
,
Lysosome
,
Metabolic pathways
💬
1件:
19
19
3
Naglazyme
(galsulfase)
1件:
Galsulfase
Galsulfase
(Synonym:
Naglazyme
)
1件:
D06565
D06565
(Name:
NAGLAZYME
)
1件:
ARSB
ARSB
💬
3件:
Glycosaminoglycan degradation
Glycosaminoglycan degradation
,
Lysosome
,
Metabolic pathways
💬
1件:
19
19
4
Naglazyme
®
1件:
Galsulfase
Galsulfase
(Synonym:
Naglazyme
)
1件:
D06565
D06565
(Name:
NAGLAZYME
)
1件:
ARSB
ARSB
💬
3件:
Glycosaminoglycan degradation
Glycosaminoglycan degradation
,
Lysosome
,
Metabolic pathways
💬
1件:
19
19