1. 球脊髄性筋萎縮症 Spinal and bulbar muscular atrophy Clinical trials / Disease details


臨床試験数 : 18 薬物数 : 15 - (DrugBank : 8) / 標的遺伝子数 : 10 - 標的パスウェイ数 : 17

  
1 trial found
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1JPRN-UMIN000026150
2017/04/2531/03/2017Safety and efficacy of mexiletine hydrochroride in spinal and bulbar muscular atrophy (SBMA) :a multicenter, randomised, double-blind, placebo-controlled trialSafety and efficacy of mexiletine hydrochroride in spinal and bulbar muscular atrophy (SBMA) :a multicenter, randomised, double-blind, placebo-controlled trial - Mexiletine in SBMA Spinal and Bulbar Muscular AtrophyMexiletine Hydrochloride 300mg daily, for 4 weeks
placebo for 4 weeks
Nagoya University Graduate School of MedicineNULLComplete: follow-up continuing20years-old80years-oldMale20Phase 2Japan