111. 先天性ミオパチー Congenital myopathy Clinical trials / Disease details

臨床試験数 : 10 / 薬物数 : 17 - (DrugBank : 5) / 標的遺伝子数 : 1 - 標的パスウェイ数 : 9

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT02035501 (ClinicalTrials.gov)	January 2014	2/7/2013	Treatment of TNNT1-Myopathy With L-Tyrosine.	Treatment of TNNT1-Myopathy With L-Tyrosine. A Double-blind, Placebo-controlled Crossover Trial.	Nemaline Myopathy	Drug: L-Tyrosine;Drug: Placebo	Hadassah Medical Organization	NULL	Enrolling by invitation	N/A	20 Years	Both	10	Phase 2	Israel