113. 筋ジストロフィー Muscular dystrophy Clinical trials / Disease details

臨床試験数 : 646 / 薬物数 : 471 - (DrugBank : 105) / 標的遺伝子数 : 59 - 標的パスウェイ数 : 170

1 trial found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	EUCTR2017-002213-60-GB (EUCTR)	08/01/2019	11/12/2018	A study to investigate the safety, tolerability, and efficacy of SGT-001 in male adolescents and chi ...	A randomized, controlled, open-label, single-ascending dose, phase I/II study to investigate the saf ...	Duchenne muscular dystrophy MedDRA version: 20.1;Level: PT;Classification code 10052655;Term: Duchen ...	Product Name: SGT-001 Product Code: rAAV9-CK8-h-µD5 INN or Proposed INN: SGT-001 Other descriptive name ...	Solid Biosciences Inc.	NULL	Authorised-recruitment may be ongoing or finished			Female: no Male: yes	32	Human pharmacology (Phase 1): yes Therapeutic exploratory (Phase 2): yes Therapeutic confirmatory - ...	United States;United Kingdom

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