138. 神経細胞移動異常症 Nerve cell migration disorder Clinical trials / Disease details


臨床試験数 : 1 薬物数 : 2 - (DrugBank : 1) / 標的遺伝子数 : 1 - 標的パスウェイ数 : 106

  
1 trial found
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1NCT05577754
(ClinicalTrials.gov)
November 28, 202210/10/2022Assessment of the Efficacy and Safety of Alpelisib (BYL719) in Pediatric and Adult Patients With Megalencephaly-CApillary Malformation Polymicrogyria Syndrome (MCAP)A Phase II Double-blind Multi-center, Placebo-controlled Trial, to Assess the Efficacy and Safety of Alpelisib (BYL719) in Pediatric and Adult Patients With Megalencephaly-CApillary Malformation Polymicrogyria Syndrome (MCAP)Megalencephaly-capillary Malformation Polymicrogyria Syndrome (MCAP)Drug: Alpelisib (BYL719);Drug: Matching placebo;Procedure: Optional lumbar punctureCentre Hospitalier Universitaire DijonNULLRecruiting2 Years40 YearsAll16Phase 2France