139. 先天性大脳白質形成不全症 Congenital cerebral hypomyelination Clinical trials / Disease details


臨床試験数 : 10 薬物数 : 7 - (DrugBank : 2) / 標的遺伝子数 : 2 - 標的パスウェイ数 : 2

  
1 trial found
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1NCT01391637
(ClinicalTrials.gov)
June 20116/7/2011Long-Term Follow-Up Study of Human Stem Cells Transplanted in Subjects With Connatal Pelizaeus-Merzbacher Disease (PMD)Long-Term Follow-Up Safety and Preliminary Efficacy Study of Human Central Nervous System Stem Cell (HuCNS-SC®) Transplantation in Subjects With Connatal Pelizaeus-Merzbacher Disease (PMD)Pelizaeus-Merzbacher Disease;PMDBiological: HuCNS-SC transplant in the lead-in phaseStemCells, Inc.NULLCompletedN/AN/AMale4United States