156. レット症候群 Rett syndrome Clinical trials / Disease details


臨床試験数 : 44 薬物数 : 61 - (DrugBank : 23) / 標的遺伝子数 : 57 - 標的パスウェイ数 : 83

  
2 trials found
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1EUCTR2012-005021-76-IT
(EUCTR)
31/01/201311/12/2012Phase 2A clinical trial conducted on children affected by Rett syndrome and who are casually administered with the experimental treatment, EPI-743, compared versus the se of placebo.A Phase 2A Randomized, Placebo Controlled Trial of EPI-743 in Children with Rett Syndrome Rett Syndrome
MedDRA version: 14.1;Level: HLGT;Classification code 10021605;Term: Inborn errors of metabolism;System Organ Class: 10027433 - Metabolism and nutrition disorders;Therapeutic area: Diseases [C] - Nutritional and Metabolic Diseases [C18]
Product Name: EPI-743
Product Code: NA
Other descriptive name: Alpha-tocotrienol quinone
EDISON PHARMACEUTICALS INC.NULLNot RecruitingFemale: yes
Male: no
Phase 2Italy
2NCT01822249
(ClinicalTrials.gov)
January 201325/3/2013Phase 2 Study of EPI-743 for Treatment of Rett SyndromeA Phase 2A Randomized, Placebo Controlled Trial of EPI-743 in Children With Rett SyndromeRett SyndromeDrug: EPI-743;Drug: PlaceboEdison Pharmaceuticals IncNULLCompletedN/A18 YearsFemale24Phase 2Italy