DDrare
Disease
Drug
Target Gene/Pathway
問合せ先
EN
164. 眼皮膚白皮症
Oculocutaneous albinism
Clinical trials
/
Disease details
臨床試験数
:
15
/
薬物数
:
54
- (
DrugBank
:
34
) /
標的遺伝子数
:
35
-
標的パスウェイ数
:
141
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TrialID
Date_
enrollment
Date_
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Scientific_title
Condition
Intervention
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sponsor
Secondary_
sponsor
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Status
Inclusion_
agemin
Inclusion_
agemax
Inclusion_
gender
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size
Phase
Countries
1
NCT00467831
(
ClinicalTrials.gov
)
April 2007
28/4/2007
Pilot Study of a Multi-Drug Regimen for Severe Pulmonary Fibrosis in Hermansky-Pudlak Syndrome
Pilot Study of a Multi-Drug Regimen for Severe Pulmonary Fibrosis in Hermansky-Pudlak Syndrome
Hermansky-Pudlak Syndrome (HPS);Pulmonary Fibrosis;Oculocutaneous Albinism;Platelet Storage Pool Deficiency;Metabolic Disease
Hermansky-Pudlak Syndrome (HPS);Pulmonary Fibrosis;Oculocutaneous Albinism;Platelet Storage Pool Def ...
Drug:
Losartan
;Drug:
Zileuton
;Drug:
N-Acetylcysteine
;Drug:
Pravastatin
;Drug:
Erythromycin
National Human Genome Research Institute (NHGRI)
NULL
Terminated
18 Years
70 Years
All
3
Phase 1/Phase 2
United States