171. ウィルソン病 Wilson disease Clinical trials / Disease details


臨床試験数 : 79 薬物数 : 77 - (DrugBank : 17) / 標的遺伝子数 : 6 - 標的パスウェイ数 : 30

  
3 trials found
No.TrialIDDate_
enrollment
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Public_titleScientific_titleConditionInterventionPrimary_
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agemin
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agemax
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PhaseCountries
1EUCTR2020-000963-22-DE
(EUCTR)
18/10/202110/03/2021A clinical trial: treatment of adult Wilson's Disease patients with gene therapyA Phase I/II, Multicenter, Non-randomized, Open Label, Adaptive Design, 5-year Follow-up, Single Dose-escalation Study of VTX-801 in Adult Patients with Wilson’s Disease - GATEWAY clinical trial Wilson's Disease
MedDRA version: 20.0;Level: LLT;Classification code 10047988;Term: Wilson's disease;System Organ Class: 100000004850;Therapeutic area: Diseases [C] - Nutritional and Metabolic Diseases [C18]
Product Name: N/A
Product Code: VTX-801
INN or Proposed INN: NA
Other descriptive name: Adeno-associated viral vector serotype 3B encoding shortened human ATP7B
Vivet Therapeutics SASNULLAuthorised-recruitment may be ongoing or finishedFemale: yes
Male: yes
16Phase 1;Phase 2United States;Denmark;Germany;United Kingdom
2NCT04537377
(ClinicalTrials.gov)
September 3, 202119/8/2020A Phase I/II Study of VTX-801 in Adult Patients With Wilson's DiseaseA Phase I/II, Multicenter, Non-randomized, Open Label, Adaptive Design, 5-year Follow-up, Single Dose-escalation Study of VTX-801 in Adult Patients With Wilson's DiseaseWilson's DiseaseGenetic: VTX-801Vivet Therapeutics SASNULLRecruiting18 Years65 YearsAll16Phase 1/Phase 2United States;Denmark;Germany;United Kingdom
3EUCTR2020-000963-22-DK
(EUCTR)
05/07/202107/05/2021A clinical trial: treatment of adult Wilson's Disease patients with gene therapyA Phase I/II, Multicenter, Non-randomized, Open Label, Adaptive Design, 5-year Follow-up, Single Dose-escalation Study of VTX-801 in AdultPatients with Wilson's Disease - GATEWAY clinical trial Wilson's Disease
MedDRA version: 20.0;Level: LLT;Classification code 10047988;Term: Wilson's disease;System Organ Class: 100000004850;Therapeutic area: Diseases [C] - Nutritional and Metabolic Diseases [C18]
Product Name: N/A
Product Code: VTX-801
INN or Proposed INN: N/A
Other descriptive name: Adeno-associated viral vector serotype 3B encoding shortened human ATP7B
Vivet Therapeutics SASNULLAuthorised-recruitment may be ongoing or finishedFemale: yes
Male: yes
16Phase 1;Phase 2United States;Denmark;Germany;United Kingdom