180. ＡＴＲ−Ｘ症候群 ATR-X syndrome Clinical trials / Disease details

臨床試験数 : 1 / 薬物数 : 3 - (DrugBank : 2) / 標的遺伝子数 : 0 - 標的パスウェイ数 : 0

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	JPRN-jRCT2051220062	14/07/2022	14/07/2022	Physician-initiated clinical trial in patients with 5-aminolevulinic acid-induced ATR-X syndrome.	Exploratory study to investigate the safety and efficacy of NPJ005 in patients with ATR-X syndrome. ...	ATR-X syndrome infant, intellectual disability, epigenetics, guanine quadruplex;D008607	Containing 5-aminolevulinic acid(5-ALA) hydrochloride and sodium ferrous citrate (SFC) Tablets (25 mg ...	Wada Takahito	NULL	Recruiting	>= 2age old	Not applicable	Male	5	Phase 2	Japan

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