19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details

臨床試験数 : 899 / 薬物数 : 684 - (DrugBank : 99) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 182

2 trials found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	EUCTR2014-005194-37-DE (EUCTR)	19/10/2015	28/04/2015	A non-therapeutic study in patients with Niemann-Pick disease type C in order to characterise the in ...	A prospective non-therapeutic study in patients diagnosed with Niemann-Pick disease type C in order ...	Niemann-Pick disease - type C MedDRA version: 18.0;Level: PT;Classification code 10029403;Term: Niem ...	Trade Name: MIglustat Product Name: Zavesca Product Code: A16AX06 INN or Proposed INN: MIGLUSTAT	Orphazyme ApS	NULL	Not Recruiting			Female: yes Male: yes	40	Phase 1	Spain;Germany;Switzerland
2	EUCTR2014-005194-37-ES (EUCTR)	13/07/2015	08/05/2015	A non-therapeutic study in patients with Niemann-Pick disease type C in order to characterise the in ...	A prospective non-therapeutic study in patients diagnosed with Niemann-Pick disease type C in order ...	Niemann-Pick disease - type C MedDRA version: 18.0;Level: PT;Classification code 10029403;Term: Niem ...	Trade Name: MIglustat Product Name: Zavesca Product Code: A16AX06 INN or Proposed INN: MIGLUSTAT	Orphazyme ApS	NULL	Not Recruiting			Female: yes Male: yes	40	Phase 1	Spain;Germany;Switzerland

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