19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details

臨床試験数 : 899 / 薬物数 : 684 - (DrugBank : 99) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 182

1 trial found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT03643562 (ClinicalTrials.gov)	June 18, 2018	19/8/2018	Niemann-Pick Type C Treatment With Adrabetadex for Symptoms of Brain and Nervous System	Open-label Evaluation of Adrabetadexin Patients With Neurologic Manifestations of Niemann-Pick Type ...	Niemann-Pick Type C Disease	Drug: Adrabetadex	Mandos LLC	NULL	Completed	4 Years	N/A	All	27	Phase 3	United States