19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details

臨床試験数 : 899 / 薬物数 : 684 - (DrugBank : 99) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 182

3 trials found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT00258011 (ClinicalTrials.gov)	December 2005	22/11/2005	Study of Aldurazyme® Replacement Therapy in Patients With Mucopolysaccharidosis I (MPS I) Disease	A Safety Confirmatory Study of JC0498 (Laronidase) in Mucopolysaccharidosis I (MPS I) Patients	Mucopolysaccharidosis I;Hurler Syndrome;Hurler-Scheie Syndrome;Scheie Syndrome	Biological: Aldurazyme (Recombinant Human Alpha-L-Iduronidase)	Genzyme, a Sanofi Company	BioMarin/Genzyme LLC	Completed	N/A	N/A	All	3	Phase 3	Japan
2	NCT00144781 (ClinicalTrials.gov)	December 2004	2/9/2005	A Dose-optimization Study of Aldurazyme® (Laronidase) in Patients With Mucopolysaccharidosis I (MPS ...	A Multicenter, Multinational, Randomized, Dose-Optimization Study of the Safety and Pharmacodynamic ...	Mucopolysaccharidosis I;Hurler's Syndrome;Hurler-Scheie Syndrome;Scheie Syndrome	Biological: Aldurazyme (Recombinant Human Alpha-L-Iduronidase)	Genzyme, a Sanofi Company	BioMarin/Genzyme LLC	Completed	N/A	N/A	All	34	Phase 4	Brazil;Canada
3	NCT00146757 (ClinicalTrials.gov)	October 2002	2/9/2005	A Study Evaluating the Safety and Pharmacokinetics of Aldurazyme® (Laronidase) in MPS I Patients Les ...	A Phase II Open-Label Clinical Trial of Recombinant Human Alpha-L-iduronidase (Aldurazyme®) to Evalu ...	Mucopolysaccharidosis I;Hurler Syndrome;Hurler-Scheie Syndrome;Scheie Syndrome	Biological: Aldurazyme (Recombinant Human Alpha-L-Iduronidase)	Genzyme, a Sanofi Company	BioMarin/Genzyme LLC	Completed	N/A	5 Years	All	20	Phase 2	France;Germany;Netherlands;United Kingdom

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