19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details


臨床試験数 : 899 薬物数 : 684 - (DrugBank : 99) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 182

  
1 trial found
No.TrialIDDate_
enrollment
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registration
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agemin
Inclusion_
agemax
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PhaseCountries
1NCT00004294
(ClinicalTrials.gov)
November 199918/10/1999Phase I Study of Retrovirally Mediated Transfer of the Human Glucocerebrosidase Gene Into Peripheral Blood Stem Cells for Autologous Transplantation in Patients With Type I Gaucher DiseaseGaucher's DiseaseGenetic: human glucocerebrosidase gene into autologous peripheral blood stem cellsNational Center for Research Resources (NCRR)National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK);University of PittsburghCompleted18 Years65 YearsBoth15Phase 1United States