19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details

臨床試験数 : 899 / 薬物数 : 684 - (DrugBank : 99) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 182

1 trial found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT00638547 (ClinicalTrials.gov)	January 2, 2008	11/3/2008	Intrathecal Enzyme Replacement for Hurler Syndrome	Intrathecal Enzyme Replacement Therapy For Patients With Mucopolysaccharidosis Type I (Hurler Syndro ...	Hurler Syndrome	Drug: IRT Laronidase	Masonic Cancer Center, University of Minnesota	NULL	Completed	6 Months	3 Years	All	26	Phase 1	United States