19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details

臨床試験数 : 899 / 薬物数 : 684 - (DrugBank : 99) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 182

6 trials found

diseases per page:

Showing 1 to 6 of 6 diseases

Filter by

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	EUCTR2010-020048-36-GB (EUCTR)	31/01/2011	17/06/2010	A safety, tolerability and preliminary efficacy study of idursulfase-IT in patients with Hunter synd ...	A Phase I/II, Randomized, Safety and Ascending Dose Ranging Study of Intrathecal Idursulfase-IT admi ...	Treatment of Hunter syndrome and cognitive impairment MedDRA version: 14.1;Level: PT;Classification ...	Product Name: Idursulfase (I2S)-IT Product Code: I2S-IT INN or Proposed INN: NA Other descriptive name: ...	Shire HGT, Inc	NULL	Not Recruiting			Female: no Male: yes	20	Human pharmacology (Phase 1): yes Therapeutic exploratory (Phase 2): yes Therapeutic confirmatory - ...	United States;United Kingdom
2	EUCTR2004-002743-27-SE (EUCTR)	11/05/2005	17/03/2005	An Open-Label Extension of Study TKT024 Evaluating Long-Term Safety and Clinical Outcomes in MPS II ...	An Open-Label Extension of Study TKT024 Evaluating Long-Term Safety and Clinical Outcomes in MPS II ...	Mucopolysaccharidosis Type II (MPS II or Hunter Syndrome) MedDRA version: 6.1;Level: PT;Classificati ...	Product Name: Idursulfase (I2S) Other descriptive name: Idursulfase	Shire Human Genetic Therapies INC.	NULL	Not Recruiting			Female: no Male: yes	96		United Kingdom;Germany;Spain;Italy;Sweden
3	EUCTR2004-002743-27-ES (EUCTR)	21/04/2005	04/04/2006	An Open-Label Extension of Study TKT024 Evaluating Long-Term Safety and Clinical Outcomes in MPS II ...	An Open-Label Extension of Study TKT024 Evaluating Long-Term Safety and Clinical Outcomes in MPS II ...	Mucopolysaccharidosis Type II (MPS II or Hunter Syndrome) MedDRA version: 6.1;Level: PT;Classificati ...	Product Name: Idursulfase (I2S) Other descriptive name: Idursulfase	TKT Inc.	NULL	Not Recruiting			Female: no Male: yes	94	Phase 3	Spain;Germany;Italy;United Kingdom;Sweden
4	EUCTR2004-002743-27-GB (EUCTR)	31/01/2005	23/02/2005	An Open-Label Extension of Study TKT024 Evaluating Long-Term Safety and Clinical Outcomes in MPS II ...	An Open-Label Extension of Study TKT024 Evaluating Long-Term Safety and Clinical Outcomes in MPS II ...	Mucopolysaccharidosis Type II (MPS II or Hunter Syndrome) MedDRA version: 6.1;Level: PT;Classificati ...	Product Name: Idursulfase (I2S) Other descriptive name: Idursulfase	TKT Inc.	NULL	Not Recruiting			Female: no Male: yes	94	Phase 3	Spain;Germany;Italy;United Kingdom;Sweden
5	EUCTR2004-002743-27-DE (EUCTR)	23/12/2004	30/11/2004	An Open-Label Extension of Study TKT024 Evaluating Long-Term Safety and Clinical Outcomes in MPS II ...	An Open-Label Extension of Study TKT024 Evaluating Long-Term Safety and Clinical Outcomes in MPS II ...	Mucopolysaccharidosis Type II (MPS II or Hunter Syndrome) MedDRA version: 6.1;Level: PT;Classificati ...	Product Name: Idursulfase (I2S) Other descriptive name: Idursulfase	Shire Human Genetic Therapies INC.	NULL	Not Recruiting			Female: no Male: yes	96		United Kingdom;Germany;Spain;Italy;Sweden
6	EUCTR2007-006044-22-PL (EUCTR)		21/04/2008	A Multi-Center, Open-Label Study Evaluating Safety and Clinical Outcomes in Hunter Syndrome Patients ...	A Multi-Center, Open-Label Study Evaluating Safety and Clinical Outcomes in Hunter Syndrome Patients ...	Mucopolysaccharidosis Type II (MPS II or Hunter Syndrome) MedDRA version: 10.1;Level: PT;Classificat ...	Trade Name: Elaprase 2mg/ml Product Name: Idursulfase (I2S) Product Code: I2S INN or Proposed INN: Idursu ...	Shire Human Genetic Therapies, Inc. (Shire HGT)	NULL	Not Recruiting			Female: no Male: yes	30	Phase 4	Poland

First Previous1Next Last