19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details


臨床試験数 : 899 薬物数 : 684 - (DrugBank : 99) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 182

  
1 trial found
No.TrialIDDate_
enrollment
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registration
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agemin
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agemax
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PhaseCountries
1NCT03721627
(ClinicalTrials.gov)
April 3, 201825/10/2018Chronic Hepatitis C Treatment in Egyptian Children With Gaucher Disease.Efficacy and Safety of Ledipasvir/Sofosbuvir Fixed Dose Combination Therapy in Treatment of Chronic Hepatitis C Infection in Egyptian Children With Gaucher DiseaseGaucher Disease;HCVDrug: Ledipasvir/SofosbuvirMansoura University Children HospitalNULLUnknown status6 Years18 YearsAll10Phase 4Egypt