19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details

臨床試験数 : 899 / 薬物数 : 684 - (DrugBank : 99) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 182

1 trial found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT01102686 (ClinicalTrials.gov)	August 2009	16/10/2009	Pyrimethamine as a Treatment for Late-Onset GM2-gangliosidosis (Tay-Sachs and Sandhoff Disease)	Proposed Investigator-Initiated Clinical Trial of Pyrimethamine as a Treatment for Late-Onset GM2-ga ...	Gangliosidoses, GM2;Sandhoff Disease;Tay-Sachs Disease	Drug: Pyrimethamine;Drug: Leucovorin	The Hospital for Sick Children	NULL	Completed	17 Years	N/A	Both	20	Phase 1/Phase 2	Canada

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