19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details

臨床試験数 : 899 / 薬物数 : 684 - (DrugBank : 99) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 182

2 trials found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT03910621 (ClinicalTrials.gov)	April 2, 2020	8/3/2019	Safety and Efficacy of Miglustat in Chinese NPC Patients	A Single Arm Uncontrolled 12 Months Clinical Study to Evaluate the Safety and Efficacy of Miglustat ...	Niemann-Pick Disease, Type C	Drug: Miglustat	Actelion	NULL	Completed	4 Years	N/A	All	17	Phase 4	China
2	EUCTR2007-007164-20-ES (EUCTR)	20/05/2008	21/02/2008	Uso racional de los tratamientos por inhibición de sustrato y enzimático sustitutivo en pacientes co ...	Uso racional de los tratamientos por inhibición de sustrato y enzimático sustitutivo en pacientes co ...	Tratamiento de la enfermedad de Gaucher MedDRA version: 9.1;Level: LLT;Classification code 10018048; ...	Trade Name: CEREZYME INN or Proposed INN: IMIGLUCERASA Trade Name: MIGLUSTAT (ZAVESCA) INN or Proposed I ...	INSTITUTO ARAGONÉS DE CIENCIAS DE LA SALUD	NULL	Not Recruiting			Female: yes Male: yes			Spain

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