19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details

臨床試験数 : 899 / 薬物数 : 684 - (DrugBank : 99) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 182

20 trials found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT01747980 (ClinicalTrials.gov)	March 2013	5/12/2012	Safety and Pharmacokinetics of Oral PRX-112 in Gaucher Disease Patients	An Exploratory, Open-label Study to Evaluate the Safety of PRX-112 and Pharmacokinetics of Oral prGC ...	Gaucher Disease	Drug: PRX-112	Protalix	NULL	Completed	18 Years	N/A	Both	16	Phase 1	Israel
2	EUCTR2011-003685-32-ES (EUCTR)	27/01/2012	13/10/2011	NA	A Multicenter Extension Study of Taliglucerase alfa in Adult Subjects with Gaucher Disease - NA	Gaucher disease MedDRA version: 14.0;Level: PT;Classification code 10018048;Term: Gaucher's disease; ...	Product Name: recombinant human glucerebrosidase Product Code: Taliglucerase Alfa INN or Proposed INN: ...	Protalix Biotherapeutics	NULL	Not Recruiting			Female: yes Male: yes	25	Phase 3	Serbia;Mexico;Canada;Spain;South Africa;Israel;Chile;Italy
3	EUCTR2011-003676-37-ES (EUCTR)	15/11/2011	14/09/2011	NA	A Multicenter Extension Study of Taliglucerase alfa in Pediatric Subjects with Gaucher Disease - NA ...	Gaucher disease MedDRA version: 14.0;Level: PT;Classification code 10018048;Term: Gaucher's disease; ...	Product Name: recombinant human glucerebrosidase Product Code: Taliglucerase Alfa INN or Proposed INN: ...	Protalix Biotherapeutics	NULL	Not Recruiting			Female: yes Male: yes	15	Phase 3	Spain;South Africa;Israel
4	EUCTR2008-005825-12-GB (EUCTR)	17/12/2009	28/04/2009	A Phase 3 Multicenter, Open-label, Switchover Trial to Assess the Safety and Efficacy of Plant Cell ...	A Phase 3 Multicenter, Open-label, Switchover Trial to Assess the Safety and Efficacy of Plant Cell ...	Gaucher Disease MedDRA version: 9.1;Level: PT;Classification code 10018048;Term: Gaucher's disease	Product Name: UPLYSO Product Code: Taliglucerase alfa Other descriptive name: recombinant human glucoc ...	Protalix Biotherapeutics	NULL	Not Recruiting			Female: yes Male: yes	30	Human pharmacology (Phase 1): no Therapeutic exploratory (Phase 2): no Therapeutic confirmatory - (P ...	Spain;Germany;Italy;United Kingdom
5	EUCTR2008-005825-12-DE (EUCTR)	10/12/2009	16/09/2009	A Phase 3 Multicenter, Open-label, Switchover Trial to Assess the Safety and Efficacy of Plant Cell ...	A Phase 3 Multicenter, Open-label, Switchover Trial to Assess the Safety and Efficacy of Plant Cell ...	Gaucher Disease MedDRA version: 9.1;Level: PT;Classification code 10018048;Term: Gaucher's disease	Product Name: UPLYSO Product Code: Taliglucerase alfa INN or Proposed INN: Taliglucerase alfa Other des ...	Protalix Biotherapeutics	NULL	Not Recruiting			Female: yes Male: yes	30	Phase 3	Spain;Germany;Italy;United Kingdom
6	EUCTR2008-005825-12-IT (EUCTR)	28/07/2009	16/09/2009	: A Phase 3 Multicenter, Open-label, Switchover Trial to Assess the Safety and Efficacy of Plant Cel ...	: A Phase 3 Multicenter, Open-label, Switchover Trial to Assess the Safety and Efficacy of Plant Cel ...	Gaucher disease MedDRA version: 9.1;Level: SOC;Classification code 10029205	Product Name: Plant Cell Recombinant Glucocerebrosidase Product Code: prGCD	PROTALIX BIOTHERAPEUTICS	NULL	Not Recruiting			Female: yes Male: yes	15	Phase 3	Germany;United Kingdom;Spain;Italy
7	EUCTR2008-005826-35-GB (EUCTR)	24/06/2009	14/04/2009	A Multicenter, Double-Blind, Extension Trial of Two Parallel Dose Groups of Plant Cell Expressed Rec ...	A Multicenter, Double-Blind, Extension Trial of Two Parallel Dose Groups of Plant Cell Expressed Rec ...	Gaucher Disease MedDRA version: 9.1;Level: PT;Classification code 10018048;Term: Gaucher's disease	Product Name: UPLYSO Product Code: Taliglucerase alfa Other descriptive name: recombinant human glucoc ...	Protalix Biotherapeutics	NULL	Not Recruiting			Female: yes Male: yes	30	Human pharmacology (Phase 1): no Therapeutic exploratory (Phase 2): no Therapeutic confirmatory - (P ...	Spain;Italy;United Kingdom
8	EUCTR2008-005826-35-IT (EUCTR)	19/06/2009	30/06/2009	A multicenter, double-blind, extension trial of two parallel dose groups of Plant cell expressed rec ...	A multicenter, double-blind, extension trial of two parallel dose groups of Plant cell expressed rec ...	Gaucher Disease	Product Name: Plant Cell Recombinant Glucocerebrosidase Product Code: prGCD Product Name: Plant Cell R ...	PROTALIX BIOTHERAPEUTICS	NULL	Not Recruiting			Female: yes Male: yes	30		United Kingdom;Spain;Italy
9	EUCTR2008-005826-35-ES (EUCTR)	04/06/2009	07/04/2009	Ensayo clínico de extensión, multicéntrico, doble ciego con dos grupos paralelos de dosis de glucoce ...	Ensayo clínico de extensión, multicéntrico, doble ciego con dos grupos paralelos de dosis de glucoce ...	Enfermedad de GaucherGaucher Disease MedDRA version: 9.1;Level: PT;Classification code 10018048;Term ...	Product Name: recombinant human glucocerebrosidase Product Code: prGCD Other descriptive name: recombi ...	Protalix Biotherapeutics	NULL	Not Recruiting			Female: yes Male: yes	30	Phase 3	Spain;Italy;United Kingdom
10	EUCTR2008-005825-12-ES (EUCTR)	04/06/2009	06/03/2009	Ensayo clinico de fase 3, multicéntrico, en abierto y con cambio de tratamiento para evaluar la segu ...	Ensayo clinico de fase 3, multicéntrico, en abierto y con cambio de tratamiento para evaluar la segu ...	Enfermedad de GaucherGaucher Disease MedDRA version: 9.1;Level: PT;Classification code 10018048;Term ...	Product Name: recombinant human glucocerebrosidase Product Code: prGCD Other descriptive name: recombi ...	Protalix Biotherapeutics	NULL	Not Recruiting			Female: yes Male: yes	15	Phase 3	Germany;United Kingdom;Spain;Italy

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