19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details

臨床試験数 : 899 / 薬物数 : 684 - (DrugBank : 99) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 182

3 trials found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT02124070 (ClinicalTrials.gov)	March 26, 2014	25/4/2014	Therapeutic Effect of Recombinant Human Growth Hormone (rhGH) on the Myopathy of Cystinosis	Therapeutic Effect of Recombinant Human Growth Hormone (rhGH) on the Myopathy of Cystinosis	Cystinosis;Myopathy	Drug: rh Growth Hormone	National Human Genome Research Institute (NHGRI)	NULL	Withdrawn	18 Years	70 Years	All	0	Phase 1/Phase 2	United States
2	NCT00748969 (ClinicalTrials.gov)	November 2008	8/9/2008	Clinical Trial of Growth Hormone in MPS I, II, and VI	Phase II/III, Randomized, Clinical Trial of the Effects of Nutropin AQ® on Growth and Bone Metabolis ...	Mucopolysaccharidosis I;Mucopolysaccharidosis II;Mucopolysaccharidosis VI	Drug: Somatropin (DNA origin)	Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center	NULL	Terminated	5 Years	17 Years	All	2	Phase 2/Phase 3	United States
3	NCT00286689 (ClinicalTrials.gov)	February 3, 2006	1/2/2006	Effects of Growth Hormone in Chronically Ill Children		Hurler Syndrome;Cerebral Palsy;Juvenile Rheumatoid Arthritis;Crohn Disease;HIV Infections	Drug: Growth Hormone;Procedure: Whole body Protein turnover;Procedure: DEXA scan	University of Texas Southwestern Medical Center	NULL	Withdrawn	3 Years	17 Years	All	0	N/A	United States

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