19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details

臨床試験数 : 899 / 薬物数 : 684 - (DrugBank : 99) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 182

25 trials found

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT03021941 (ClinicalTrials.gov)	July 31, 2019	23/9/2016	Pharmacokinetics, Pharmacodynamics And Safety Study Of Elelyso(tm) In Pediatric Subjects With Type 1 ...	A MULTICENTER, OPEN LABEL, PHARMACOKINETICS, PHARMACODYNAMICS AND SAFETY STUDY OF ELELYSO(TM) (TALIG ...	Type 1 Gaucher Disease	Drug: Elelyso 60 units/kg	Pfizer	NULL	Withdrawn	N/A	12 Years	All	0	Phase 4	United States
2	NCT01747980 (ClinicalTrials.gov)	March 2013	5/12/2012	Safety and Pharmacokinetics of Oral PRX-112 in Gaucher Disease Patients	An Exploratory, Open-label Study to Evaluate the Safety of PRX-112 and Pharmacokinetics of Oral prGC ...	Gaucher Disease	Drug: PRX-112	Protalix	NULL	Completed	18 Years	N/A	Both	16	Phase 1	Israel
3	EUCTR2011-003685-32-ES (EUCTR)	27/01/2012	13/10/2011	NA	A Multicenter Extension Study of Taliglucerase alfa in Adult Subjects with Gaucher Disease - NA	Gaucher disease MedDRA version: 14.0;Level: PT;Classification code 10018048;Term: Gaucher's disease; ...	Product Name: recombinant human glucerebrosidase Product Code: Taliglucerase Alfa INN or Proposed INN: ...	Protalix Biotherapeutics	NULL	Not Recruiting			Female: yes Male: yes	25	Phase 3	Serbia;Mexico;Canada;Spain;South Africa;Israel;Chile;Italy
4	EUCTR2011-003676-37-ES (EUCTR)	15/11/2011	14/09/2011	NA	A Multicenter Extension Study of Taliglucerase alfa in Pediatric Subjects with Gaucher Disease - NA	Gaucher disease MedDRA version: 14.0;Level: PT;Classification code 10018048;Term: Gaucher's disease; ...	Product Name: recombinant human glucerebrosidase Product Code: Taliglucerase Alfa INN or Proposed INN: ...	Protalix Biotherapeutics	NULL	Not Recruiting			Female: yes Male: yes	15	Phase 3	Spain;South Africa;Israel
5	NCT01411228 (ClinicalTrials.gov)	September 2011	4/8/2011	A Multicenter Extension Study of Taliglucerase Alfa in Pediatric Subjects With Gaucher Disease	A Multicenter Extension Study of Taliglucerase Alfa in Pediatric Subjects With Gaucher Disease	Gaucher Disease	Drug: Taliglucerase alfa	Pfizer	NULL	Completed	2 Years	18 Years	All	15	Phase 3	Israel;Paraguay;South Africa
6	NCT01422187 (ClinicalTrials.gov)	August 2011	22/8/2011	A Multicenter Extension Study of Taliglucerase Alfa in Adult Subjects With Gaucher Disease	A Multicenter Extension Study of Taliglucerase Alfa in Adult Subjects With Gaucher Disease	Gaucher Disease	Drug: Taliglucerase alfa	Pfizer	NULL	Completed	18 Years	N/A	All	19	Phase 3	NULL
7	NCT01132690 (ClinicalTrials.gov)	August 2010	26/5/2010	A Safety and Efficacy Study of Two Dose Levels of Taliglucerase Alfain Pediatric Subjects With Gauch ...	A Multicenter, Double-blind, Randomized Safety and Efficacy Study of Two Dose Levels of Taligluceras ...	Gaucher Disease	Drug: Taliglucerase alfa	Pfizer	NULL	Completed	2 Years	17 Years	All	11	Phase 4	Israel;Paraguay;South Africa;United States
8	EUCTR2008-005825-12-GB (EUCTR)	17/12/2009	28/04/2009	A Phase 3 Multicenter, Open-label, Switchover Trial to Assess the Safety and Efficacy of Plant Cell ...	A Phase 3 Multicenter, Open-label, Switchover Trial to Assess the Safety and Efficacy of Plant Cell ...	Gaucher Disease MedDRA version: 9.1;Level: PT;Classification code 10018048;Term: Gaucher's disease	Product Name: UPLYSO Product Code: Taliglucerase alfa Other descriptive name: recombinant human glucoc ...	Protalix Biotherapeutics	NULL	Not Recruiting			Female: yes Male: yes	30	Human pharmacology (Phase 1): no Therapeutic exploratory (Phase 2): no Therapeutic confirmatory - (P ...	Spain;Germany;Italy;United Kingdom
9	EUCTR2008-005825-12-DE (EUCTR)	10/12/2009	16/09/2009	A Phase 3 Multicenter, Open-label, Switchover Trial to Assess the Safety and Efficacy of Plant Cell ...	A Phase 3 Multicenter, Open-label, Switchover Trial to Assess the Safety and Efficacy of Plant Cell ...	Gaucher Disease MedDRA version: 9.1;Level: PT;Classification code 10018048;Term: Gaucher's disease	Product Name: UPLYSO Product Code: Taliglucerase alfa INN or Proposed INN: Taliglucerase alfa Other des ...	Protalix Biotherapeutics	NULL	Not Recruiting			Female: yes Male: yes	30	Phase 3	Spain;Germany;Italy;United Kingdom
10	EUCTR2008-005825-12-IT (EUCTR)	28/07/2009	16/09/2009	: A Phase 3 Multicenter, Open-label, Switchover Trial to Assess the Safety and Efficacy of Plant Cel ...	: A Phase 3 Multicenter, Open-label, Switchover Trial to Assess the Safety and Efficacy of Plant Cel ...	Gaucher disease MedDRA version: 9.1;Level: SOC;Classification code 10029205	Product Name: Plant Cell Recombinant Glucocerebrosidase Product Code: prGCD	PROTALIX BIOTHERAPEUTICS	NULL	Not Recruiting			Female: yes Male: yes	15	Phase 3	Germany;United Kingdom;Spain;Italy

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