19. ライソゾーム病 Lysosomal storage disease Clinical trials / Disease details

臨床試験数 : 899 / 薬物数 : 684 - (DrugBank : 99) / 標的遺伝子数 : 51 - 標的パスウェイ数 : 182

1 trial found

diseases per page:

Showing 1 to 1 of 1 diseases

Filter by

No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	JPRN-UMIN000009758	2013/06/24	15/01/2013	Development of treosulfan-based conditioning regimen for congenital metabolic diseases; Phase I stud ...	Development of treosulfan-based conditioning regimen for congenital metabolic diseases; Phase I stud ...	Mucopolysaccharidosis type I (Herler syndrome), type II (Hunter syndrome)	Treosulfan 14 g/m2, intravenous, day -6 -5 -4	Tokai University School of Medicine	1. School of Human Health Science Faculty of Medicine Kyoto University2. Department of Pediatrics, J ...	Complete: follow-up complete	Not applicable	Not applicable	Male and Female	12	Phase 1	Japan

First Previous1Next Last