244. メープルシロップ尿症 Maple syrup urine disease Clinical trials / Disease details

臨床試験数 : 1 / 薬物数 : 1 - (DrugBank : 1) / 標的遺伝子数 : 0 - 標的パスウェイ数 : 0

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No.	TrialID	Date_ enrollment	Date_ registration	Public_title	Scientific_title	Condition	Intervention	Primary_ sponsor	Secondary_ sponsor	Recruitment_ Status	Inclusion_ agemin	Inclusion_ agemax	Inclusion_ gender	Target_ size	Phase	Countries
1	NCT01529060 (ClinicalTrials.gov)	February 2013	6/2/2012	Phenylbutyrate Therapy for Maple Syrup Urine Disease	A Double-Blind, Randomized, Placebo-Controlled, Crossover Trial of Phenylbutyratein the Treatment of ...	Maple Syrup Urine Disease	Drug: Phenylbutyrate;Drug: Placebo powder	Brendan Lee	NULL	Completed	3 Years	N/A	All	20	Phase 2/Phase 3	United States